Sfoglia per Autore
Enzyme replacement therapy in adult-onset type II glycogenosis
2007-01-01 Ravaglia, SABRINA MARIA; Repetto, Alessandra; Rossi, Miriam; Costa, Alfredo; Danesino, Cesare; Rossi, Miriam; Fratino, P; Lozza, A; Alfonsi, E; Bastianello, Stefano; Moglia, Arrigo
Recombinant alpha-glucosidase in adult-onset type II glycogenosis: The experience with the first Italian patient, from expanded access programmes to marketing authorization
2007-01-01 Ravaglia, SABRINA MARIA; Repetto, Alessandra; Bini, P; Costa, Alfredo; Rossi, Miriam; Lozza, A; Alfonsi, E; Rossi, Miriam; DE FILIPPI, Paola; Fratino, P; Moglia, Arrigo; Danesino, Cesare
Adult-onset type II glycogenosis (GSDII): Clinical spectrum and enzyme replacement therapy (ERT)
2007-01-01 Repetto, Alessandra; Bini, P; Ravaglia, S; Rossi, Miriam; Costa, Alfredo; Alfonsi, E; Lozza, A; Danesino, Cesare; Minelli, Antonella; Rossi, Miriam; Moglia, Arrigo
Early-onset ptosis in type II glycogenosis
2007-01-01 Repetto, Alessandra; Ravaglia, SABRINA MARIA; Rossi, Miriam; Danesino, Cesare; Rossi, Miriam; Costa, Alfredo; Moglia, Arrigo
Recombinant alglucosidase alpha (rhGAA) in adult-onset type II glycogenosis (GSDII): A follow-up study before and after treatment
2008-01-01 Ravaglia, SABRINA MARIA; Danesino, Cesare; Rossi, Miriam; Moglia, Arrigo
RECOMBINANT ALGLUCOSIDASE ALFA IN ADULT-ONSET GLYCOGENOSIS TYPE II: A FOLLOW-UP STUDY BEFORE AND AFTER TREATMENT
2008-01-01 Ravaglia, SABRINA MARIA; Repetto, Alessandra; Costa, Alfredo; Fratino, P; Rossi, Miriam; Moglia, Arrigo; Danesino, Cesare
Outcome after Two Years of Enzyme Replacement Therapy (ERT) in 29 Patients with Late-Onset Type II Glycogenosis (GSDII)
2009-01-01 Ravaglia, SABRINA MARIA; Moglia, Arrigo; Rossi, Miriam; Costa, Alfredo; Rigoldi, M.; Bembi, B.; Danesino, Cesare
Titolo | Data di pubblicazione | Autore(i) | File |
---|---|---|---|
Enzyme replacement therapy in adult-onset type II glycogenosis | 1-gen-2007 | Ravaglia, SABRINA MARIA; Repetto, Alessandra; Rossi, Miriam; Costa, Alfredo; Danesino, Cesare; Rossi, Miriam; Fratino, P; Lozza, A; Alfonsi, E; Bastianello, Stefano; Moglia, Arrigo | |
Recombinant alpha-glucosidase in adult-onset type II glycogenosis: The experience with the first Italian patient, from expanded access programmes to marketing authorization | 1-gen-2007 | Ravaglia, SABRINA MARIA; Repetto, Alessandra; Bini, P; Costa, Alfredo; Rossi, Miriam; Lozza, A; Alfonsi, E; Rossi, Miriam; DE FILIPPI, Paola; Fratino, P; Moglia, Arrigo; Danesino, Cesare | |
Adult-onset type II glycogenosis (GSDII): Clinical spectrum and enzyme replacement therapy (ERT) | 1-gen-2007 | Repetto, Alessandra; Bini, P; Ravaglia, S; Rossi, Miriam; Costa, Alfredo; Alfonsi, E; Lozza, A; Danesino, Cesare; Minelli, Antonella; Rossi, Miriam; Moglia, Arrigo | |
Early-onset ptosis in type II glycogenosis | 1-gen-2007 | Repetto, Alessandra; Ravaglia, SABRINA MARIA; Rossi, Miriam; Danesino, Cesare; Rossi, Miriam; Costa, Alfredo; Moglia, Arrigo | |
Recombinant alglucosidase alpha (rhGAA) in adult-onset type II glycogenosis (GSDII): A follow-up study before and after treatment | 1-gen-2008 | Ravaglia, SABRINA MARIA; Danesino, Cesare; Rossi, Miriam; Moglia, Arrigo | |
RECOMBINANT ALGLUCOSIDASE ALFA IN ADULT-ONSET GLYCOGENOSIS TYPE II: A FOLLOW-UP STUDY BEFORE AND AFTER TREATMENT | 1-gen-2008 | Ravaglia, SABRINA MARIA; Repetto, Alessandra; Costa, Alfredo; Fratino, P; Rossi, Miriam; Moglia, Arrigo; Danesino, Cesare | |
Outcome after Two Years of Enzyme Replacement Therapy (ERT) in 29 Patients with Late-Onset Type II Glycogenosis (GSDII) | 1-gen-2009 | Ravaglia, SABRINA MARIA; Moglia, Arrigo; Rossi, Miriam; Costa, Alfredo; Rigoldi, M.; Bembi, B.; Danesino, Cesare |
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